Child giving high-five
PATIENT SUPPORT

Partnering with patients throughout their health journeys

100s
Partner advocacy organizations worldwide
15
Industry-leading support programs for U.S. patients
70+
Global online educational resources

Our commitment to patients extends beyond developing therapies. We also provide support and advocacy programs, educational materials, and other resources to inform and empower patients and their families.

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Commitment to patients
Our work extends beyond developing therapies. We’re committed to helping patients obtain access to our treatments by offering a variety of support programs to eligible patients.
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Patient advocacy
We work with organizations around the world who share our mission to advocate for the needs of patients.
Gaucher disease patient family
Lysosomal storage disorder registries
These large, often multinational databases of clinical data, aggregate knowledge to help improve understanding of rare diseases that would be otherwise difficult to study.
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Reporting side effects
Gaucher patient
Patient access to treatment
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Educational websites

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